Pharma News - Chemdiv

MBX Biosciences’ Hypoparathyroidism Drug Candidate Gains Orphan Drug Status

MBX Biosciences’ investigational drug MBX 2109 received Orphan Drug designation from the FDA for treatment of hypoparathyroidism.

Vertex’s VX-548 Gets Breakthrough Therapy Designation for Acute Pain

Vertex Pharmaceuticals’ investigational oral drug VX-548 has received FDA’s Breakthrough Therapy designation for the treatment of patients with moderate-to-severe acute pain. ...

FDA Expands Approval of Janssen’s Stelara for Pediatric Psoriatic Arthritis

The FDA has expanded its approval to Janssen’s Stelara (ustekinumab) for treatment of pediatric patients six years and older with psoriatic arthritis.

US government buys 66m doses of Moderna’s Omicron booster

The Biden administration has confirmed its plans to start a booster vaccination campaign in the autumn, and placed a $1.74 billion order for 66 million doses of an updated version of Moderna’s Sp...

Ipsen Invests Potential $1.6B to Turbo-Charge Marengo's Path to the Clinic

Marengo Therapeutics and Ipsen announced Monday that they have entered into a strategic, multi-year partnership to usher two of Marengo’s precision T cell immuno-oncology candidates into the clin...

Sarepta Plans on Submitting BLA for Duchenne Gene Therapy

Sarepta Therapeutics said that it plans to submit a Biologics License Application (BLA) for accelerated approval of its investigational gene therapy candidate SRP-9001 (delandistrogene moxeparvove...

FDA Grants Orphan Drug Designation to Omeros’ MASP-3 Inhibitor OMS906 for Treatment of Paroxysmal Nocturnal Hemoglobinuria

Omeros Corporation today announced that OMS906 has received orphan drug designation from the U.S. Food and Drug Administration (FDA) for the treatment of paroxysmal nocturnal hemoglobinuria (PNH).&...

Growing evidence supports the link between air pollution and dementia

Imperial researchers contribute to a report highlighting how air pollution contributes to dementia and a decline in mental ability.

FDA Greenlights Jynneos Monkeypox Vaccine for Additional Manufacturing

The FDA has given the green light for additional manufacturing of Bavarian Nordic’s Jynneos vaccine at the company’s fill and finish facility in Denmark. ...

DeepMind’s AlphaFold tool has determined the structures of around 200 million proteins

From today, determining the 3D shape of almost any protein known to science will be as simple as typing in a Google search.

Stem Cell Transplant Cures Oldest HIV Patient

California-based biomedical research institution City of Hope revealed Wednesday that the oldest person living with HIV has achieved clinical remission after undergoing stem cell transplantation at...

GSK's Benlysta Becomes First Biologic Approved for Lupus Nephritis in Kids

British multinational GlaxoSmithKline announced Wednesday that the U.S. Food and Drug Administration gave its Benlysta (belimumab) the greenlight for use against active lupus nephritis in children ...

Pharma News, 2022